PicnicHealth | Research Studies

Your role in research starts here


INSPIRE-D Study](/content/make-an-impact/inspire-d/index.html)

Enrolling

Hereditary Angioedema (HAE)

DAWNZERA™ (donidalorsen)

The INSPIRE-D Observational Study will evaluate the real-world effectiveness and safety of DAWNZERA™ (donidalorsen) in people with HAE. By participating, you'll help researchers learn more about DAWNZERA™ (donidalorsen).

Activities


Compass Study](/content/make-an-impact/compass/index.html)

Enrolling

Methylmalonic acidemia (MMA) and propionic acidemia (PA)

This observational study is designed to better understand the impact of MMA and PA on families. By collecting medical records and brief survey responses, researchers can understand how the condition is managed, how symptoms evolve, and where support is most needed.

Activities


Navigate-CIDP Study](/content/make-an-impact/argenx-navigate-cidp/index.html)

Enrolling

Chronic Inflammatory Demyelinating Polyradiculoneuropathy (CIDP)

The NAVIGATE-CIDP Study looks at how CIDP affects a person’s daily life, based on symptoms and quality-of-life surveys. It also tracks treatment patterns—like why people switch medications—and builds a foundation for future research.

Activities


Beacon SLE Study](/content/make-an-impact/beacon-sle/index.html)

Enrolling

Systemic lupus erythematosus (SLE)

Benlysta® (belimumab)

The BEACON-SLE Study is a real-world non-interventional research study that looks at the experiences of people with systemic lupus erythematosus (SLE) and how they respond to treatment with Benlysta® (belimumab) in real life.

Activities


OBSERVE-NMO Study](/content/make-an-impact/observe-nmo/index.html)

Enrolling

Neuromyelitis optica spectrum disorder (NMOSD)

UPLIZNA® (inebilizumab-cdon)

The OBSERVE-NMO Study is a real-world observational research study that looks at the experiences of people with NMOSD who take UPLIZNA® (inebilizumab-cdon) to improve future care.

Activities


Tepli-QUEST Study](/content/make-an-impact/tepli-quest/index.html)

Enrolling

Stage 2 Type 1 Diabetes

The Tepli-QUEST Study is a real-world observational research study that looks at the experiences of people with Stage 2 type 1 diabetes (T1D) who have received teplizumab compared to those who have not.

Activities


ORBIT-CIDP Study](/content/make-an-impact/orbit-cidp/index.html)

Enrolling

Chronic Inflammatory Demyelinating Polyneuropathy (CIDP)

The ORBIT-CIDP study collects real-world data to better understand CIDP, including condition progression, treatment effectiveness, and patient experiences.

Activities


OPUS-W Study](/content/make-an-impact/az-opus-w/index.html)

Enrolling

Transthyretin-Mediated Amyloidosis (ATTR)

WAINUA™

The OPUS-W registry combines anonymized data from patients with ATTR taking WAINUA™ to gain a clearer picture of their daily life.

Activities


PLEDGE Study](/content/make-an-impact/pledge/index.html)

Enrolling

Paroxysmal Nocturnal Hemoglobinuria (PNH)

VOYDEYA™ (danicopan)

The PLEDGE Study is an observational research effort to gather insight into the day-to-day lives of individuals who recently initiated danicopan to manage PNH.

Activities


CAHtalog Study](/content/make-an-impact/cah/index.html)

Enrolling

Congenital Adrenal Hyperplasia (CAH)

CAHtalog’s mission is to advance CAH clinical research and in turn improve the quality of life for those living with classic CAH.

Activities


Long-Term Follow-Up Study](https://app.picnichealth.com/)

Enrolling

CAR-T Cell Therapy

This study will follow your health over time to better understand the long-term effects and outcomes after receiving gene-modified T-cell therapy.

Activities


ASMD Accelerate Study](/content/make-an-impact/asmd-wylder-nation/index.html)

Enrolling

Acid Sphingomyelinase Deficiency

This study is hoping to understand how ASMD progresses over time, as well as how the disease is actually managed and treated in the real-world.

Activities